3 of my kids have sickle cell. I keep up on all the research and currently we are trying to get one of my sons into a trial. The trial is for a gene therapy treatment done by Vertex (vrtx) and crispr (crsp). they have completed their fda submission. It is essentially a cure for sickle cell and another blood disease beta thalassemia. I expect the approval to happen by mid-fall if other drugs approval times can be used as a measuring stick and this is expected to be the most expensive treatment ever ( in excess of 2 million dollars for 1 treatment). vrtx has a 60%/40% arrangement with crsp.
I am not a financial analyst and what I'm telling you is for entertainment only (unless your loved one has sickle cell, then you should totally look into the treatment). With that said, I'm going to buy as many options expiring in january as I can afford on either. I fully expect this will be the last year my son will have sickle cell and I expect to make a decent sum from those options.